Rare Genetic Disorders: How CRISPR Could Offer Hope for Previously Incurable Diseases
Genetic disorders are conditions that result from anomalies in an individual’s DNA. While some genetic disorders are common, many are rare and can have devastating effects on those affected and their families. These rare genetic disorders, often categorized as orphan diseases, present significant challenges for diagnosis, treatment, and research. However, the advent of advanced genomic technologies, particularly CRISPR-Cas9 gene editing, offers new hope for the treatment of these previously incurable diseas
